New drug trial hopes to tame rare skin disease

NCT ID NCT06539507

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This early-stage trial tests a new drug called BCX17725 in healthy volunteers and people with Netherton syndrome, a rare genetic skin condition. The study aims to check safety, how the drug moves through the body, and whether it can reduce skin redness and scaling. About 78 participants will take part across four parts, with the final part also looking at effectiveness over 12 weeks.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

BCX17725

What this could lead to

If successful, this could point toward a treatment that controls the severe skin symptoms of Netherton syndrome.

What could go wrong

This is a very early Phase 1 trial, so safety and effectiveness are not yet known. The drug may not work or could have side effects.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Netherton syndrome

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Dawes Fretzin Clinical Research Group, LLC

    RECRUITING

    Indianapolis, Indiana, 46250, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Erasmus Universitair Medisch Centrum (EMC)

    RECRUITING

    Rotterdam, 3015 GD, Netherlands

  • Hôpital Saint-Louis

    RECRUITING

    Paris, 75010, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Maastricht Universitair Medisch Centrum (MUMC+)

    RECRUITING

    Maastricht, 6229 HX, Netherlands

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Northwestern Dermatology CTU

    RECRUITING

    Chicago, Illinois, 60611, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Nucleus Network

    COMPLETED

    Brisbane, Queensland, 4006, Australia

  • Stanford University School of Medicine

    NOT_YET_RECRUITING

    Palo Alto, California, 94304, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Therapeutics Clinical Research

    RECRUITING

    San Diego, California, 92123, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Universitätsklinikum Heidelberg

    NOT_YET_RECRUITING

    Heidelberg, 69120, Germany

  • Veracity Clinical Research

    RECRUITING

    Brisbane, Queensland, 4102, Australia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Westmead Hospital - Department of Dermatology

    RECRUITING

    Sydney, New South Wales, 2145, Australia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Yale Center for Clinical Investigation

    RECRUITING

    New Haven, Connecticut, 06519, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••