New hope for kids with rare autoimmune disease

NCT ID NCT06321601

Summary

This study is testing a drug called avacopan in children aged 6 to 18 who have a rare autoimmune condition called ANCA-associated vasculitis. The main goal is to see if adding avacopan to standard treatments helps children achieve and maintain disease remission over one year. Researchers will also monitor safety, how the drug works in children's bodies, and even how the medicine tastes to kids.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Akron Childrens Hospital

    RECRUITING

    Akron, Ohio, 44308, United States

  • Alberta Childrens Hospital

    RECRUITING

    Calgary, Alberta, T3B 6A8, Canada

  • CHU Sainte Justine

    RECRUITING

    Montreal, Quebec, H3T 1C5, Canada

  • Centre Hospitalier Universitaire de Bordeaux - Hopital Pellegrin

    RECRUITING

    Bordeaux, 33076, France

  • Cleveland Clinic Foundation

    RECRUITING

    Cleveland, Ohio, 44195, United States

  • Cohen Children Medical Center

    RECRUITING

    Lake Success, New York, 11042, United States

  • Dzieciecy Szpital Kliniczny im. Jozefa Polikarpa Brudzinskiego w Warszawie

    RECRUITING

    Warsaw, 02-091, Poland

  • Emory University

    RECRUITING

    Atlanta, Georgia, 30322, United States

  • Fakultni nemocnice v Motole

    RECRUITING

    Prague, 150 06, Czechia

  • Hopital Necker

    RECRUITING

    Paris, 75015, France

  • Hopital Necker Enfants Malades

    RECRUITING

    Paris, 75015, France

  • Hospices Civils de Lyon Hopital Femme Mere Enfant

    RECRUITING

    Bron, 69677, France

  • Hospital Sant Joan de Deu

    RECRUITING

    Esplugues de Llobregat, Catalonia, 08950, Spain

  • Hospital Universitari Vall d Hebron

    RECRUITING

    Barcelona, Catalonia, 08035, Spain

  • Hospital Universitario 12 de Octubre

    RECRUITING

    Madrid, 28041, Spain

  • Narodny ustav detskych chorob

    RECRUITING

    Bratislava, 833 40, Slovakia

  • Riley Hospital for Children

    RECRUITING

    Indianapolis, Indiana, 46202, United States

  • Semmelweis Egyetem

    RECRUITING

    Budapest, 1094, Hungary

  • Stollery Childrens Hospital

    RECRUITING

    Edmonton, Alberta, T6G 1C9, Canada

  • Szegedi Tudomanyegyetem Szent-Gyorgyi Albert Klinikai Kozpont Altalanos Orvostudomanyi Kar

    RECRUITING

    Szeged, 6720, Hungary

  • Texas Childrens Hospital

    RECRUITING

    Houston, Texas, 77030, United States

  • Universitair Ziekenhuis Gent

    RECRUITING

    Ghent, 9000, Belgium

  • Universitair Ziekenhuis Leuven - Gasthuisberg

    RECRUITING

    Leuven, 3000, Belgium

  • University of Minnesota Masonic Childrens Hospital Discovery Clinic

    RECRUITING

    Minneapolis, Minnesota, 55454, United States

  • University of North Carolina

    RECRUITING

    Chapel Hill, North Carolina, 27599, United States

  • University of Pittsburgh Medical Center Childrens Hospital of Pittsburgh

    RECRUITING

    Pittsburgh, Pennsylvania, 15224, United States

  • Uniwersytecki Szpital Dzieciecy w Krakowie

    RECRUITING

    Krakow, 30-663, Poland

  • Uniwersyteckie Centrum Kliniczne

    RECRUITING

    Gdansk, 80-952, Poland

  • Vseobecna fakultni nemocnice v Praze

    RECRUITING

    Prague, 128 08, Czechia

  • Wake Forest University Health Sciences

    RECRUITING

    Charlotte, North Carolina, 28203, United States

Conditions

Explore the condition pages connected to this study.