New combo therapy shows promise for Steroid-Resistant ITP

NCT ID NCT05438875

First seen Jun 26, 2026 · Last updated Jun 26, 2026

Summary

This completed phase 3 trial tested whether adding all-trans retinoic acid (ATRA) to eltrombopag works better than eltrombopag alone for adults with immune thrombocytopenia (ITP) that did not respond to steroids. The study enrolled 96 participants and measured sustained platelet count improvement at 18 months. The goal is to find a more effective treatment option for this chronic bleeding disorder.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

all-trans retinoic acid (ATRA) and eltrombopag

What this could lead to

If successful, this combination could offer a more effective treatment option for people with immune thrombocytopenia (ITP) that does not respond to steroids, helping maintain safe platelet levels.

What could go wrong

This is a relatively small phase 3 trial (96 participants), and results may not apply to all ITP patients. The combination may cause side effects, and long-term benefits are not guaranteed.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

autoimmune thrombocytopenic purpura Purpura, Thrombocytopenic, Idiopathic thrombocytopenia due to immune destruction

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Beijing Tongren hospital

    Beijing, Beijing Municipality, China

  • Department of Hematology, Beijing Friendship Hospital, Capital Medical University

    Beijing, China

  • Department of Hematology, Beijing Hospital

    Beijing, China

  • Department of Hematology, Senior Department of Hematology, the Fifth Medical Center of PLA General Hospital

    Beijing, China

  • Peking University Insititute of Hematology, Peking University People's Hospital

    Beijing, Beijing Municipality, 100010, China