Gene therapy trial for rare heart condition halted before it began
NCT ID NCT06483802
First seen Nov 01, 2025 · Last updated Jun 13, 2026 · Updated 33 times
Summary
This study aimed to test a new gene therapy called ASP2016 for heart problems in people with Friedreich Ataxia, a rare genetic disease. Participants would have received one infusion of the therapy and taken steroids to prevent immune reactions. The study was withdrawn before enrolling anyone, so no results are available.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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