Common cough medicine tested for rare brain disease in kids

NCT ID NCT07285369

Summary

This study is testing whether high doses of Ambroxol, a medication commonly used for coughs, can help children with Gaucher Disease Type 3. Twelve children aged 3-18 will take the medication daily for 6 months, with an option to continue for another year. Researchers want to see if it's safe and if it improves movement problems and other symptoms of this rare genetic condition.

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Contacts and locations

Locations

  • The Children's Hospital

    Lahore, Pakistan

Conditions

Explore the condition pages connected to this study.