GAUCHER DISEASE, TYPE 3
Clinical trials for GAUCHER DISEASE, TYPE 3 explained in plain language.
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Doctors test Life-Saving enzyme treatment for babies before they are born
Disease control Recruiting nowThis early-stage study is testing whether giving enzyme replacement therapy to fetuses still in the womb is safe and feasible. It aims to treat rare, severe genetic disorders that often cause life-threatening complications before or shortly after birth. The hope is that treating …
Matched conditions: GAUCHER DISEASE, TYPE 3
Phase: PHASE1 • Sponsor: University of California, San Francisco • Aim: Disease control
Last updated Mar 30, 2026 14:32 UTC
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Scientists scan brains to unlock clues in rare neurological disease
Knowledge-focused Recruiting nowThis study aims to understand how Gaucher Disease Type 3 affects the brain in adults. Researchers will use a special brain scan (MRS) to measure chemicals in the brains of up to 5 participants. The goal is to find markers that could one day help measure if treatments are working.
Matched conditions: GAUCHER DISEASE, TYPE 3
Sponsor: University of Minnesota • Aim: Knowledge-focused
Last updated Mar 16, 2026 15:24 UTC