GAUCHER DISEASE TYPE 3

Clinical trials for GAUCHER DISEASE TYPE 3 explained in plain language.

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Trials to join now! 3 Not yet recruiting 2 Not yet finished but already full! 1 Terminated 1

Could a pill replace infusions for gaucher brain symptoms?

Disease control Ongoing

This phase 2 trial tests an oral drug called venglustat, given alongside the standard enzyme therapy Cerezyme, in adults with Gaucher disease type 3 (a rare genetic disorder affecting the body and brain). The study has four parts: first, it checks spinal fluid biomarkers to disti…

Matched conditions: GAUCHER DISEASE TYPE 3

Phase: PHASE2 • Sponsor: Genzyme, a Sanofi Company • Aim: Disease control

Last updated Jul 12, 2026 00:00 UTC

GAUCHER DISEASE TYPE 3

Get alerted when new GAUCHER DISEASE TYPE 3 trials appear

Could a pill replace infusions for gaucher brain symptoms?