Cough medicine repurposed for rare brain disease in kids
Disease control
Completed
This study tested high doses of Ambroxol, a common cough medicine, in 12 children aged 3 to 18 with Type 3 Gaucher disease, a rare genetic disorder affecting the brain and body. The goal was to see if it is safe and can improve movement problems like ataxia. The trial took place …
Sponsor: Agyany Pharma LTD • Aim: Disease control
Last updated Aug 26, 2026 00:00 UTC