Could a common cough medicine help kids with a rare brain disease?
Disease control
Terminated
This study tested high doses of ambroxol, a common cough medicine, in 12 children aged 3 to 18 with type III Gaucher disease, a rare genetic disorder affecting the brain and body. The goal was to see if it could improve movement and coordination safely. The study was stopped earl…
Phase: NA • Sponsor: Agyany Pharma LTD • Aim: Disease control
Last updated May 26, 2026 12:07 UTC