New registry aims to unlock secrets of kidney disease that starts in childhood

NCT ID NCT04338048

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study creates a registry to collect health information from people with Autosomal Dominant Polycystic Kidney Disease (ADPKD), the most common genetic cause of kidney failure. While ADPKD was once thought to only affect adults, researchers now know it begins in childhood, but there are no clear guidelines for managing it early. By gathering medical data and optional blood or urine samples from 300 participants, the study hopes to fill that gap and build better online resources for patients and families.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

What this could lead to

If successful, this registry could provide the first evidence-based guidelines for managing ADPKD in children and help families understand the disease earlier.

What could go wrong

This is an observational registry, not a treatment trial, so it will not directly change outcomes for participants. Results depend on how many people join and share data over time.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

autosomal dominant polycystic kidney disease

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19146, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Children's National Hospital

    RECRUITING

    Washington D.C., District of Columbia, 20010, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Cohen Children's Medical Center

    ENROLLING_BY_INVITATION

    New Hyde Park, New York, 11042, United States

  • Mayo Clinic

    RECRUITING

    Rochester, Minnesota, 55902, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••