One-Time gene shot aims to tame rare copper disorder
Disease control
Ongoing
This early-stage trial tests a single dose of VTX-801 gene therapy in 4 adults with Wilson's disease, a rare condition where copper builds up in the body. The goal is to see if the treatment is safe and can help control copper levels, possibly allowing patients to stop their usua…
Phase: PHASE1, PHASE2 • Sponsor: Vivet Therapeutics SAS • Aim: Disease control
Last updated Jun 27, 2026 09:00 UTC