This is an early-stage study testing a single dose of an experimental gene therapy called VTX-801 in adults with Wilson's Disease. The main goal is to check if the treatment is safe and to see how it affects the body's copper levels over five years. Researchers will give the ther…
Phase: PHASE1, PHASE2 • Sponsor: Vivet Therapeutics SAS • Aim: Disease control
Last updated Mar 27, 2026 12:40 UTC