Gene therapy hopes to tame rare copper disorder
Disease control
Ongoing
This study tests a new gene therapy called VTX-801 for adults with Wilson's disease, a rare condition where copper builds up in the body. Four participants receive a single dose to see if it is safe and can help control copper levels, possibly allowing them to stop other treatmen…
Phase: PHASE1, PHASE2 • Sponsor: Vivet Therapeutics SAS • Aim: Disease control
Last updated Apr 26, 2026 20:03 UTC