Experimental drug tested for boys with Muscle-Wasting disease
Disease control
Terminated
This study tested an experimental drug called PGN-EDO51 in boys with Duchenne muscular dystrophy who have a specific genetic mutation. The main goal was to check if the drug is safe and how the body processes it when given through an IV over time. Researchers also measured whethe…
Phase: PHASE2 • Sponsor: PepGen Inc • Aim: Disease control
Last updated Apr 02, 2026 08:27 UTC