New drug shows promise for muscle stiffness in rare disease
Symptom relief
Completed
This early-stage study tested a single dose of a new drug called PGN-EDODM1 in 24 adults with myotonic dystrophy type 1 (DM1), a condition that causes muscle weakness and stiffness. The main goal was to check if the drug is safe and how the body processes it. Researchers monitore…
Phase: PHASE1 • Sponsor: PepGen Inc • Aim: Symptom relief
Last updated May 11, 2026 20:41 UTC