Tracking treatment for rare genetic disease
Disease control
ENROLLING_BY_INVITATION
This study is observing how well enzyme replacement therapy works for people with Fabry disease in Russia. Researchers will follow 100 patients who are already receiving this standard treatment as part of their regular care. They will collect data on symptoms, kidney and heart fu…
Sponsor: NPO Petrovax • Aim: Disease control
Last updated Apr 02, 2026 01:41 UTC