Tracking treatment for rare genetic disease

NCT ID NCT06880250

ENROLLING_BY_INVITATION Disease control Sponsor: NPO Petrovax Source: ClinicalTrials.gov ↗

Summary

This study is observing how well enzyme replacement therapy works for people with Fabry disease in Russia. Researchers will follow 100 patients who are already receiving this standard treatment as part of their regular care. They will collect data on symptoms, kidney and heart function, and side effects over 6 to 18 months to understand the therapy's real-world effectiveness.

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Contacts and locations

Locations

  • #10

    Krasnodar, Russia

  • #11

    Ufa, Russia

  • #12

    Ivanovo, Russia

  • #13

    Astrakhan, Russia

  • #15

    Orenburg, Russia

  • #16

    Gubkin, Russia

  • #17

    Omsk, Russia

  • #18

    Kurgan, Russia

  • #19

    Kaa-Khem, Russia

  • #2

    Rostov-on-Don, Russia

  • #21

    Grozny, Russia

  • #22

    Stavropol, Russia

  • #23

    Polevskoy, Russia

  • #24

    Ryazan, Russia

  • #26

    Irkutsk, Russia

  • #27

    Barnaul, Russia

  • #3

    Simferopol, Russia

  • #4

    Rostov-on-Don, Russia

  • #5

    Voronezh, Russia

  • #6

    Chelyabinsk, Russia

  • #7

    Borovichi, Russia

  • #8

    Saint Petersburg, Russia

  • #9

    Perm, Russia

Conditions

Explore the condition pages connected to this study.