New hope for toddlers with rare hormone disorder?
Disease control
Not yet recruiting
This study tests a drug called crinecerfont in 20 children aged 3 months to 4 years with classic congenital adrenal hyperplasia (CAH). The goal is to see if the drug is safe and tolerable. Participants must already be on stable hydrocortisone treatment. The study is not yet recru…
Phase: PHASE2 • Sponsor: Neurocrine Biosciences • Aim: Disease control
Last updated May 12, 2026 13:41 UTC