Study seeks to measure how treatment affects development in devastating childhood disease
Knowledge-focused
ENROLLING_BY_INVITATION
This study aims to understand how a rare, fatal childhood brain disease called CLN2 Batten disease affects children's development. Researchers will track 30 children, comparing those receiving a treatment called cerliponase alfa to those who are untreated. The goal is to measure …
Sponsor: Jessica Scherr • Aim: Knowledge-focused
Last updated Apr 02, 2026 06:56 UTC