Could a simple amino acid ease rare brain disorders?
Symptom relief
Not yet recruiting
This study tests a drug called N-acetyl-L-leucine for people aged 4 and older with CACNA1A gene disorders, which can cause coordination problems, dizziness, and migraines. About 60 participants will receive either the drug or a placebo, then switch, to see if it improves movement…
Phase: PHASE3 • Sponsor: IntraBio Inc • Aim: Symptom relief
Last updated Jun 27, 2026 13:03 UTC