Experimental drug tested for rare neurological disease
Disease control
Terminated
This study tested an experimental drug called N-Acetyl-L-Leucine for people with Ataxia-Telangiectasia (A-T), a rare genetic disorder that affects coordination and the immune system. The main goal was to see if the drug was safe and if it could help improve symptoms like walking,…
Phase: PHASE2 • Sponsor: IntraBio Inc • Aim: Disease control
Last updated Mar 30, 2026 14:30 UTC