Gene therapy injection aims to restore sight in rare blindness
Disease control
Recruiting now
This study is testing an experimental gene therapy called GS010 for people with a rare, inherited form of vision loss called ND4 Leber Hereditary Optic Neuropathy (LHON). Researchers are injecting the therapy into both eyes of participants to see if it can improve vision and how …
Phase: PHASE2 • Sponsor: GenSight Biologics • Aim: Disease control
Last updated Mar 09, 2026 14:23 UTC