Gene therapy injection aims to restore sight in rare eye disease
Disease control
Recruiting now
This study tests a new drug called GS010, given as an injection into the eye, for people with Leber Hereditary Optic Neuropathy (LHON), a genetic condition that causes rapid vision loss. The goal is to see if the treatment can improve eyesight and boost the activity of energy-pro…
Phase: PHASE2 • Sponsor: GenSight Biologics • Aim: Disease control
Last updated May 08, 2026 12:02 UTC