Groundwork study paves way for future DMD gene therapy trials
Knowledge-focused
Recruiting now
This study aims to track how Duchenne Muscular Dystrophy (DMD) naturally progresses in boys aged 4 to 9 years old over 6 to 36 months. Researchers will measure muscle function, mobility, heart health, and breathing to establish baseline data. This information will help design and…
Sponsor: Genethon • Aim: Knowledge-focused
Last updated Mar 30, 2026 14:29 UTC