First human test of new cell therapy for inherited nerve disease
Disease control
Completed
This was a very early, small study to check the safety of a new cell therapy called EN001 for people with Charcot-Marie-Tooth disease type 1A (CMT1A), a genetic nerve disorder. Six adult participants received two doses of EN001 to find the highest safe amount. Researchers monitor…
Phase: PHASE1 • Sponsor: ENCell • Aim: Disease control
Last updated Mar 25, 2026 14:08 UTC