New drug EN001 tested for rare nerve disease – early safety results in
Disease control
Completed
This early-phase trial tested the safety of a new drug called EN001 in 6 adults with Charcot-Marie-Tooth disease type 1A, a genetic nerve disorder that causes muscle weakness and numbness. The main goal was to see if the drug caused serious side effects. Researchers also looked f…
Phase: PHASE1 • Sponsor: ENCell • Aim: Disease control
Last updated May 17, 2026 13:23 UTC