New drug EN001 tested for rare nerve disease – early safety results in
NCT ID NCT06328712
First seen Jan 10, 2026 · Last updated May 15, 2026 · Updated 19 times
Summary
This early-phase trial tested the safety of a new drug called EN001 in 6 adults with Charcot-Marie-Tooth disease type 1A, a genetic nerve disorder that causes muscle weakness and numbness. The main goal was to see if the drug caused serious side effects. Researchers also looked for signs that the drug might slow the disease, but this was a small, short study focused on safety, not a cure.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Samsung Medical Center
Seoul, South Korea
Conditions
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