Experimental drug aims to fix faulty kidney protein in rare genetic disease
Disease control
Completed
This small, early-stage study tested whether daily injections of an experimental drug called ELX-02 are safe and can improve kidney health in adults with a specific genetic form of Alport Syndrome. The drug is designed to help the body produce a crucial protein that is missing du…
Phase: PHASE2 • Sponsor: Eloxx Pharmaceuticals, Inc. • Aim: Disease control
Last updated Apr 01, 2026 14:41 UTC