Scientists launch 3-Year hunt for clues to heart risks in rare disease
Knowledge-focused
Ongoing
This study aims to better understand how a group of rare genetic disorders, called mucopolysaccharidoses (MPS), affects heart and blood vessel health over time. Researchers will follow 30 patients for three years, using annual heart ultrasounds, neck artery scans, and blood tests…
Sponsor: Children's Hospital of Orange County • Aim: Knowledge-focused
Last updated Mar 11, 2026 14:54 UTC