New approach aims to boost effectiveness of PKU drug
Disease control
Not yet recruiting
This study is testing whether adding a medication called methotrexate to the existing PKU treatment Palynziq can help control the condition better. It aims to see if methotrexate reduces the body's immune reaction to Palynziq, potentially making the treatment more tolerable and e…
Phase: PHASE4 • Sponsor: BioMarin Pharmaceutical • Aim: Disease control
Last updated Mar 30, 2026 14:29 UTC