New hope for rare epilepsy: ION283 trial launches
Disease control
Recruiting now
This study tests a new drug called ION283 in 10 people aged 10 to 18 with Lafora disease, a rare and severe form of epilepsy. The drug is given through a spinal injection to see if it is safe and can help control symptoms. The goal is to slow the disease and improve daily functio…
Phase: PHASE1, PHASE2 • Sponsor: Berge Minassian • Aim: Disease control
Last updated Apr 26, 2026 19:35 UTC