New hope for rare epilepsy: drug ION283 enters human trials
NCT ID NCT06609889
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tests a new drug called ION283 in 10 people aged 10 to 18 with Lafora disease, a rare and severe form of epilepsy. The drug is given via a spinal injection to see if it is safe and can help control seizures and other symptoms. All participants will receive the same dose, and the study will monitor side effects and changes in disease severity over two years.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Study contacts
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Contact
Email: •••••@•••••
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Contact
Email: •••••@•••••
Locations
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Childrens Health
RECRUITINGDallas, Texas, 75235, United States
Contact Email: •••••@•••••
Contact Email: •••••@•••••