New hope for rare epilepsy: drug ION283 enters human trials
Disease control
Recruiting now
This study tests a new drug called ION283 in 10 people aged 10 to 18 with Lafora disease, a rare and severe form of epilepsy. The drug is given via a spinal injection to see if it is safe and can help control seizures and other symptoms. All participants will receive the same dos…
Phase: PHASE1, PHASE2 • Sponsor: Berge Minassian • Aim: Disease control
Last updated Jun 27, 2026 08:05 UTC