Apr Applied Pharma Research S.a.

This completed trial tested whether PKU GOLIKE, a special food for managing PKU, works better than standard amino acid protein substitutes at controlling blood phenylalanine levels. Sixteen children with PKU, aged 5 to 16, took part in a crossover study where they tried both prod…

This study checks if a new liquid form of sapropterin (RLF-OD032) works the same as the approved powder (Kuvan) in 42 healthy adults. Participants receive a single dose of each version under fed conditions, and blood samples are taken to compare drug levels. The goal is to see if…