Agios Pharmaceuticals, Inc.
Clinical trials sponsored by Agios Pharmaceuticals, Inc., explained in plain language.
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New hope for kids with thalassemia: drug may cut need for blood transfusions
Disease control Not yet recruitingThis study tests an oral drug called mitapivat in children aged 1 to under 18 with transfusion-dependent thalassemia, a blood disorder requiring regular red blood cell transfusions. The goal is to see if mitapivat can reduce the number of transfusions needed compared to a placebo…
Phase: PHASE3 • Sponsor: Agios Pharmaceuticals, Inc. • Aim: Disease control
Last updated May 17, 2026 07:04 UTC
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New pill could boost hemoglobin in kids with thalassemia
Disease control Not yet recruitingThis study tests whether the drug mitapivat can raise hemoglobin levels in children aged 1 to 17 with alpha- or beta-thalassemia who do not need regular blood transfusions. About 45 participants will receive either mitapivat or a placebo daily for 24 weeks. The main goal is to se…
Phase: PHASE3 • Sponsor: Agios Pharmaceuticals, Inc. • Aim: Disease control
Last updated May 15, 2026 11:56 UTC