Agios Pharmaceuticals, Inc.
Clinical trials sponsored by Agios Pharmaceuticals, Inc., explained in plain language.
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New PKU drug enters first human safety testing
Disease control Not yet recruitingThis is an early safety study for a new oral drug called AG-181 in adults with phenylketonuria (PKU). The main goal is to see if the drug is safe and well-tolerated in 20 participants. Researchers will also measure how the drug moves through the body and its effect on blood pheny…
Phase: PHASE1 • Sponsor: Agios Pharmaceuticals, Inc. • Aim: Disease control
Last updated Mar 30, 2026 14:34 UTC
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New hope for sickle cell patients facing kidney failure
Disease control Not yet recruitingThis study is testing whether an oral drug called mitapivat can help protect the kidneys of people with sickle cell disease. It will enroll about 40 participants who already show signs of early kidney damage. Researchers will measure protein levels in urine over 6 months to see i…
Phase: PHASE2 • Sponsor: Agios Pharmaceuticals, Inc. • Aim: Disease control
Last updated Mar 17, 2026 12:55 UTC