Agios Pharmaceuticals, Inc.

This study aimed to understand the long-term safety and effectiveness of the drug mitapivat for adults with pyruvate kinase deficiency, a rare genetic blood disorder. It was an extension study for 90 participants who had already benefited from mitapivat in earlier trials. The mai…

This was an early-stage study to check the safety and see how the body processes a new drug called AG-181. It involved 88 healthy volunteers who took either the drug or a placebo. The main goal was to see if the drug was safe and to measure how much of it got into the bloodstream…