Hope for a devastating childhood disease: drug trial aims to halt progression
Disease control
Completed
This study tested a drug called baricitinib for children with Aicardi Goutières Syndrome (AGS), a rare and severe genetic disorder that causes brain damage and affects many organs. The goal was to see if the drug, taken for a year, could safely reduce harmful inflammation and hel…
Phase: PHASE2 • Sponsor: Adeline Vanderver, MD • Aim: Disease control
Last updated Mar 23, 2026 15:17 UTC