Could a drug calm the immune attack in aicardi goutières syndrome?
NCT ID NCT03921554
First seen Jan 07, 2026 · Last updated Jun 16, 2026 · Updated 24 times
Summary
This study tested the drug baricitinib in 54 people with Aicardi Goutières Syndrome (AGS), a rare genetic disorder where the immune system attacks the brain. The goal was to see if the drug could safely slow or stop the disease by reducing harmful inflammation. Researchers measured changes in brain function over 52 weeks using a special scale.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
Conditions
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