X-LINKED ADRENOLEUKODYSTROPHY
Clinical trials for X-LINKED ADRENOLEUKODYSTROPHY explained in plain language.
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Doctors test One-Time gene fix for devastating childhood brain disease
⭐️ CURE ⭐️ Recruiting nowThis trial is testing a new gene therapy for X-linked adrenoleukodystrophy (X-ALD), a severe genetic brain disease that often affects young boys. Researchers are giving patients a one-time treatment that delivers a corrected gene directly into the body, aiming to fix the underlyi…
Matched conditions: X-LINKED ADRENOLEUKODYSTROPHY
Phase: NA • Sponsor: Shenzhen Geno-Immune Medical Institute • Aim: ⭐️ CURE ⭐️
Last updated Mar 19, 2026 14:55 UTC
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Massive global hunt for answers to devastating brain diseases
Knowledge-focused Recruiting nowThis study aims to collect medical information and biological samples from 12,000 people worldwide with rare genetic brain disorders called leukodystrophies. Researchers will use this data to better understand these diseases, improve diagnosis, and identify targets for future tre…
Matched conditions: X-LINKED ADRENOLEUKODYSTROPHY
Sponsor: Children's Hospital of Philadelphia • Aim: Knowledge-focused
Last updated Mar 25, 2026 14:09 UTC