WOLFRAM SYNDROME

Clinical trials for WOLFRAM SYNDROME explained in plain language.

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Trials to join now! 1 Not yet recruiting 1 Not yet finished but already full! 1 Completed 1

New drug trial aims to slow rare wolfram syndrome

Disease control Ongoing

This study tests an experimental drug called AMX0035 in 12 adults with Wolfram syndrome, a rare genetic disorder that causes diabetes and vision loss. The goal is to see if the drug can protect insulin-producing cells and is safe over up to 4 years. Participants take the drug by …

Matched conditions: WOLFRAM SYNDROME

Phase: PHASE2 • Sponsor: Amylyx Pharmaceuticals Inc. • Aim: Disease control

Last updated May 15, 2026 11:55 UTC

WOLFRAM SYNDROME

Get alerted when new WOLFRAM SYNDROME trials appear

New drug trial aims to slow rare wolfram syndrome