TRANSFUSION-DEPENDENT THALASSEMIA
Clinical trials for TRANSFUSION-DEPENDENT THALASSEMIA explained in plain language.
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Drug cocktail may cut transfusions for kids with thalassemia
Disease control CompletedThis study tested whether giving children with transfusion-dependent thalassemia a combination of hydroxyurea and thalidomide works better than either drug alone. Ninety children aged 3-18 were split into three groups: one getting both drugs, one getting only hydroxyurea, and one…
Matched conditions: TRANSFUSION-DEPENDENT THALASSEMIA
Phase: PHASE4 • Sponsor: Bangabandhu Sheikh Mujib Medical University, Dhaka, Bangladesh • Aim: Disease control
Last updated Jun 27, 2026 14:00 UTC
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CRISPR gene editing offers hope for thalassemia patients to ditch transfusions
Disease control CompletedThis study tested a single treatment using CRISPR gene editing to modify a person's own blood stem cells, aiming to help people with severe beta-thalassemia stop needing regular blood transfusions. 59 participants received the therapy and were monitored for safety and how long th…
Matched conditions: TRANSFUSION-DEPENDENT THALASSEMIA
Phase: PHASE2, PHASE3 • Sponsor: Vertex Pharmaceuticals Incorporated • Aim: Disease control
Last updated Jun 27, 2026 08:03 UTC
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Scientists track lifespan of transfused blood in sickle cell kids
Knowledge-focused CompletedThis study looked at how long donor red blood cells survive in children with sickle cell disease who get regular blood transfusions. Researchers labeled a small part of the transfused blood with a harmless marker and tracked it over time. The goal was to better understand why som…
Matched conditions: TRANSFUSION-DEPENDENT THALASSEMIA
Phase: PHASE1 • Sponsor: Marianne Yee • Aim: Knowledge-focused
Last updated Jun 27, 2026 12:37 UTC