TRANSFUSION-DEPENDENT BETA-THALASSEMIA
Clinical trials for TRANSFUSION-DEPENDENT BETA-THALASSEMIA explained in plain language.
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Pill aims to free patients from constant blood transfusions
Disease control OngoingThis Phase 3 trial tested whether an oral medication called mitapivat could reduce the need for regular blood transfusions in adults with severe forms of thalassemia. 258 participants who required frequent transfusions were randomly assigned to receive either mitapivat or a place…
Matched conditions: TRANSFUSION-DEPENDENT BETA-THALASSEMIA
Phase: PHASE3 • Sponsor: Agios Pharmaceuticals, Inc. • Aim: Disease control
Last updated Apr 01, 2026 14:41 UTC
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Could Low-Oxygen blood storage ease the burden of lifelong transfusions?
Disease control ENROLLING_BY_INVITATIONThis study is observing adults with transfusion-dependent thalassemia who are already receiving blood stored in a special low-oxygen system as part of their regular care. The goal is to see if this new storage method helps reduce how much blood they need, improves their energy le…
Matched conditions: TRANSFUSION-DEPENDENT BETA-THALASSEMIA
Sponsor: University Research Institute for the Study of Genetic & Malignant Disorders in Childhood • Aim: Disease control
Last updated Apr 01, 2026 14:41 UTC