SPINAL MUSCULAR ATROPHY (SMA)

Clinical trials for SPINAL MUSCULAR ATROPHY (SMA) explained in plain language.

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Trials to join now! 10 Not yet recruiting 3 Not yet finished but already full! 1

Two-Drug combo aims to build muscle, boost movement in SMA

Disease control Ongoing

This study is testing whether adding a new investigational drug called RO7204239 to the approved SMA drug risdiplam is safe and more effective. RO7204239 is designed to block a protein that limits muscle growth, potentially helping muscles get bigger and stronger. The trial will …

Matched conditions: SPINAL MUSCULAR ATROPHY (SMA)

Phase: PHASE2, PHASE3 • Sponsor: Hoffmann-La Roche • Aim: Disease control

Last updated Mar 30, 2026 14:31 UTC

SPINAL MUSCULAR ATROPHY (SMA)

Get alerted when new SPINAL MUSCULAR ATROPHY (SMA) trials appear

Two-Drug combo aims to build muscle, boost movement in SMA