SEVERE HEMOPHILIA A
Clinical trials for SEVERE HEMOPHILIA A explained in plain language.
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Can a new hemophilia drug protect Patients' joints and boost activity?
Disease control OngoingThis study is checking if a preventive treatment called emicizumab helps protect joints and allows for more physical activity in teens and adults with moderate to severe hemophilia A. It will follow 136 participants for up to 3 years, using ultrasounds, activity trackers, and que…
Matched conditions: SEVERE HEMOPHILIA A
Phase: PHASE4 • Sponsor: Hoffmann-La Roche • Aim: Disease control
Last updated Mar 31, 2026 12:11 UTC
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New hope for babies with severe bleeding disorder
Disease control OngoingThis study is testing a preventive drug called emicizumab in babies under 1 year old who have severe hemophilia A, a serious genetic bleeding disorder. The main goal is to see if regular injections can safely reduce the number of bleeding episodes these infants experience. After …
Matched conditions: SEVERE HEMOPHILIA A
Phase: PHASE3 • Sponsor: Hoffmann-La Roche • Aim: Disease control
Last updated Mar 27, 2026 12:37 UTC
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New hope for families facing rare childhood illnesses
Symptom relief ENROLLING_BY_INVITATIONThis study is testing a support program called FACE-Rare for families caring for children with serious, rare diseases. The program aims to help identify and meet families' needs for support, improve caregivers' quality of life, and assist with planning for future medical decision…
Matched conditions: SEVERE HEMOPHILIA A
Phase: NA • Sponsor: Children's National Research Institute • Aim: Symptom relief
Last updated Mar 24, 2026 12:02 UTC