SANDHOFF DISEASE

Clinical trials for SANDHOFF DISEASE explained in plain language.

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Trials to join now! 3 Not yet finished but already full! 1 Completed 1 Terminated 2

Scientists map the progression of rare childhood brain diseases

Knowledge-focused Completed

This study aimed to understand how neurological symptoms like walking and speech difficulties change over time in children with rare genetic disorders called GM1 or GM2 gangliosidosis. It followed 31 children with late-infantile or juvenile onset of the disease, using doctor asse…

Matched conditions: SANDHOFF DISEASE

Sponsor: Azafaros A.G. • Aim: Knowledge-focused

Last updated Mar 27, 2026 12:39 UTC

SANDHOFF DISEASE

Get alerted when new SANDHOFF DISEASE trials appear

Scientists map the progression of rare childhood brain diseases