Rare disease study paves way for future treatments

NCT ID NCT02851862

First seen Mar 12, 2026 · Last updated May 16, 2026 · Updated 9 times

Summary

This study followed 10 people with late onset Tay-Sachs disease to learn how the condition changes over six months. Researchers measured balance, coordination, and brain chemicals to better understand the disease. The goal was to gather information that will help design future clinical trials for potential treatments.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Massachusetts General Hospital

    Boston, Massachusetts, 02114, United States

Conditions

Explore the condition pages connected to this study.