PROTEUS SYNDROME

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Trials to join now! 1 Not yet finished but already full! 1

Hope for rare overgrowth disorder: daily pill shows promise in early trial

Disease control Ongoing

This phase 2 trial tests whether a daily pill called miransertib can slow or stop the abnormal tissue overgrowth seen in Proteus syndrome, a rare genetic condition. About 38 people aged 3 and older will take the drug for up to 4 years. Researchers will measure changes in foot ove…

Matched conditions: PROTEUS SYNDROME

Phase: PHASE2 • Sponsor: National Human Genome Research Institute (NHGRI) • Aim: Disease control

Last updated Jun 27, 2026 14:01 UTC

PROTEUS SYNDROME

Get alerted when new PROTEUS SYNDROME trials appear

Hope for rare overgrowth disorder: daily pill shows promise in early trial