Hope for rare overgrowth disorder: new drug trial launches
NCT ID NCT04316546
First seen Nov 01, 2025 · Last updated May 15, 2026 · Updated 32 times
Summary
This study tests a daily pill called miransertib in people with Proteus syndrome, a rare condition causing abnormal tissue growth. The goal is to see if the drug can safely slow or stop this overgrowth. About 45 participants aged 3 and older will take the drug for up to 4 years, with regular checkups and scans to track progress.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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National Institutes of Health Clinical Center
RECRUITINGBethesda, Maryland, 20892, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
Explore the condition pages connected to this study.