MICROCEPHALY
Clinical trials for MICROCEPHALY explained in plain language.
Never miss a new study
Get alerted when new MICROCEPHALY trials appear
Sign up with your email to follow new studies for MICROCEPHALY, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Gene therapy aims to halt rare childhood paralysis disorder
Disease control Recruiting nowThis trial tests a single injection of MELPIDA, a gene therapy that delivers a working copy of the AP4M1 gene directly into the spinal fluid of children with SPG50. SPG50 is a rare genetic condition that causes muscle stiffness, intellectual disability, and developmental delays. …
Matched conditions: MICROCEPHALY
Phase: PHASE1, PHASE2 • Sponsor: Elpida Therapeutics SPC • Aim: Disease control
Last updated Jul 10, 2026 00:00 UTC
-
Can intensive Play-Based therapy help kids with brain injuries move better?
Disease control Recruiting nowThis study looks at how well a special intensive therapy called ACQUIRE Therapy works for children with motor problems caused by conditions like cerebral palsy, autism, or brain injury. The therapy involves many hours of play-based exercises each day, often with a cast or splint …
Matched conditions: MICROCEPHALY
Sponsor: Virginia Polytechnic Institute and State University • Aim: Disease control
Last updated Jun 27, 2026 08:12 UTC
-
Scientists launch study to unravel rare MEHMO syndrome
Knowledge-focused Recruiting nowThis observational study follows 150 people with MEHMO syndrome or related conditions to better understand how the disease progresses. Researchers will collect medical history, imaging, and lab samples to find biological markers that could help monitor the disease. No treatment i…
Matched conditions: MICROCEPHALY
Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) • Aim: Knowledge-focused
Last updated Jun 27, 2026 14:02 UTC