METHYLMALONIC ACIDEMIA

Clinical trials for METHYLMALONIC ACIDEMIA explained in plain language.

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Trials to join now! 2 Not yet finished but already full! 1 Terminated 1

MRNA therapy for rare metabolic disease shows early promise but study halted

Disease control Terminated

This study tested an experimental mRNA medicine called mRNA-3705 in 18 people with a rare genetic condition called methylmalonic acidemia (MMA), which causes harmful acid buildup in the body. The goal was to see if the treatment is safe and can lower MMA levels. The study was ter…

Matched conditions: METHYLMALONIC ACIDEMIA

Phase: PHASE1, PHASE2 • Sponsor: ModernaTX, Inc. • Aim: Disease control

Last updated May 17, 2026 16:43 UTC

METHYLMALONIC ACIDEMIA

Get alerted when new METHYLMALONIC ACIDEMIA trials appear

MRNA therapy for rare metabolic disease shows early promise but study halted