METHYLMALONIC ACIDEMIA
Clinical trials for METHYLMALONIC ACIDEMIA explained in plain language.
Never miss a new study
Get alerted when new METHYLMALONIC ACIDEMIA trials appear
Sign up with your email to follow new studies for METHYLMALONIC ACIDEMIA, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
New mRNA therapy aims to control rare metabolic disease Long-Term
Disease control Recruiting nowThis study is testing the long-term safety of an mRNA therapy called mRNA-3705 in people with methylmalonic acidemia (MMA), a rare genetic disorder that prevents the body from breaking down certain proteins and fats. Participants have already been in earlier studies of this drug.…
Matched conditions: METHYLMALONIC ACIDEMIA
Phase: PHASE1, PHASE2 • Sponsor: ModernaTX, Inc. • Aim: Disease control
Last updated Jun 27, 2026 08:06 UTC
-
Scientists launch deep dive into rare metabolic disease MMA
Knowledge-focused Recruiting nowThis study aims to learn more about methylmalonic acidemia (MMA) and related disorders by observing people with these conditions over time. Researchers will track complications, perform tests like blood draws and MRIs, and look for new genetic causes. The goal is to better unders…
Matched conditions: METHYLMALONIC ACIDEMIA
Sponsor: National Human Genome Research Institute (NHGRI) • Aim: Knowledge-focused
Last updated Jul 02, 2026 00:00 UTC