METACHROMATIC LEUKODYSTROPHY (MLD)
Clinical trials for METACHROMATIC LEUKODYSTROPHY (MLD) explained in plain language.
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Experimental spinal injection aims to keep kids with rare disease moving
Disease control CompletedThis study tests a drug called SHP611, given as a spinal injection, in 36 children with late infantile metachromatic leukodystrophy (MLD), a rare and severe brain disease. The main goal is to see if the treatment helps children keep their ability to walk and move for as long as p…
Matched conditions: METACHROMATIC LEUKODYSTROPHY (MLD)
Phase: PHASE2 • Sponsor: Shire • Aim: Disease control
Last updated Jul 12, 2026 00:00 UTC
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New hope for rare brain disease: Long-Term safety data collected
Disease control CompletedThis study followed 24 people with metachromatic leukodystrophy (MLD), a rare and serious brain disease, who were already receiving an experimental drug called HGT-1110. The main goal was to check for side effects and immune reactions over a long period. Researchers wanted to see…
Matched conditions: METACHROMATIC LEUKODYSTROPHY (MLD)
Phase: PHASE1, PHASE2 • Sponsor: Shire • Aim: Disease control
Last updated Jun 27, 2026 12:23 UTC