METACHROMATIC LEUKODYSTROPHY (MLD)

Clinical trials for METACHROMATIC LEUKODYSTROPHY (MLD) explained in plain language.

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Not yet finished but already full! 1 Completed 1

New spinal injection may help kids with rare brain disease keep moving

Disease control Ongoing

This study tests a medicine called SHP611 for children with late infantile metachromatic leukodystrophy (MLD), a rare and serious brain disease. The main goal is to see if injecting SHP611 into the spinal fluid helps children keep the ability to walk and move for longer. About 36…

Matched conditions: METACHROMATIC LEUKODYSTROPHY (MLD)

Phase: PHASE2 • Sponsor: Shire • Aim: Disease control

Last updated May 14, 2026 12:06 UTC

METACHROMATIC LEUKODYSTROPHY (MLD)

Get alerted when new METACHROMATIC LEUKODYSTROPHY (MLD) trials appear

New spinal injection may help kids with rare brain disease keep moving