MENKES DISEASE

Clinical trials for MENKES DISEASE explained in plain language.

Never miss a new study

Get alerted when new MENKES DISEASE trials appear

Sign up with your email to follow new studies for MENKES DISEASE, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.

Our safety recommendation!

By submitting, you agree to our Terms of use

Trials to join now! 1 Not yet finished but already full! 3 Completed 1

Could a blood pressure drug improve daily life for rare disease survivors?

Symptom relief Completed

This study tested whether the drug Northera (droxidopa) is safe and helpful for adults with Menkes disease or Occipital Horn Syndrome who have trouble with low blood pressure and other symptoms of dysautonomia. Three participants took either the drug or a placebo in a crossover d…

Matched conditions: MENKES DISEASE

Phase: PHASE1, PHASE2 • Sponsor: Stephen G. Kaler, MD • Aim: Symptom relief

Last updated Jun 27, 2026 12:07 UTC

MENKES DISEASE

Get alerted when new MENKES DISEASE trials appear

Could a blood pressure drug improve daily life for rare disease survivors?